GAITHERSBURG, Md., Nov. 2, 2016 /PRNewswire/ -- Vtesse, Inc., a company committed to developing drugs that will benefit patients with extremely rare, life-threatening diseases, announced today that the MHRA, an executive agency of the Department of Health in the United Kingdom that is responsible for ensuring that medicines and medical devices are acceptably safe, has granted a Promising Innovative Medicine ("PIM") designation for VTS-270, Vtesse's investigational drug for children with Niemann-Pick Type C1 disease ("NPC"). "It is extremely gratifying to the NPC community, to the team at Vtesse, and to all of the individuals, organizations, and institutions who are tirelessly working on the development of VTS-270 that it has been recognized by the MHRA as a scientific innovation that may improve the lives of people living with NPC," said Ben Machielse, Drs., President and Chief Executive Officer of Vtesse, Inc. "It takes considerable collaboration and dedication to advance the clinical study and regulatory processes for drug development in the rare disease space. Above all, we thank all the parents who have supported the development of VTS-270." "This UK PIM designation, coupled with the U.S. FDA Breakthrough Therapy Designation granted earlier this year, demonstrates the strength of the preliminary clinical data of NPC treatment with VTS-270," added Kevin Johnson, PhD, MBA, Vice President, Regulatory Affairs at Vtesse. "Both designations afford us enhanced regulatory opportunities, which we will rely on as we complete our rigorous Phase 2b/3 clinical trial and seek regulatory approvals to bring this drug to market as quickly as possible." A PIM Designation is an early indication that a medicinal product is a promising candidate for the Early Access to Medicines Scheme ("EAMS"), in the treatment, diagnosis or prevention of life-threatening or seriously debilitating conditions with unmet need. The EAMS is a UK program run by the MHRA that aims to give patients with life-threatening conditions access to specified pre-license medicines when there is a clear medical need.