- an oral presentation titled “Neuropathy progression rate in patients with familial amyloidotic polyneuropathy” in the “ATTR: Diagnosis and pathogenesis” plenary session being held on Wednesday, April 30 from 11:30 a.m. – 1:00 p.m. ET;
- an oral presentation titled “Further analysis of phase II trial of patisiran, a novel RNAi therapeutic for the treatment of familial amyloidotic polyneuropathy” in the “ATTR: Prognosis and therapy” plenary session being held on Wednesday, April 30 from 2:30 p.m. – 4:30 p.m. ET; and,
- a poster titled “Preclinical Evaluation of RNAi Therapeutics for the Treatment of ATTR: An Update” on Wednesday, April 30.
Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), a leading RNAi therapeutics company, announced today that its scientists and collaborators will present pre-clinical and clinical data with patisiran (ALN-TTR02) and ALN-TTRsc – RNAi therapeutics targeting transthyretin (TTR) for the treatment of TTR-mediated amyloidosis (ATTR) – at the XIV th International Symposium on Amyloidosis (ISA) being held April 27 – May 1, 2014 in Indianapolis, Indiana. Amongst other new data, the company presentations include results from a 283-patient natural history study of ATTR patients with familial amyloidotic polyneuropathy (FAP) that document the rate of disease progression. Presentations and posters from Alnylam scientists and collaborators at the meeting include: