Vertex Pharmaceuticals ( VRTX) presents important final data from the phase II study of VX-809/Kalydeco at the 2012 North American Cystic Fibrosis (NACF) conference on Thursday, Oct. 11. I'm flying to Orlando, Fla., for the conference to cover the presentation and Vertex's investor meeting. Partial top-line results from this VX-809/Kalydeco study were announced over the summer (more on those data below). At the NACF meeting, we'll see a breakdown of response from the three different VX-809 dose groups, individual patient data and perhaps more insight into why the reduction in sweat chloride was smaller than expected (and whether this matters or not). Vertex has already made the decision to move the 600 mg dose of VX-809+Kalydeco into a phase III study to start early next year.
@chasingthealpha asks, "How is $OSIR almost $360M in mcap? This is junk." Osiris Therapeutics ( OSIR) shouldn't trade for much more than cash -- let's call it $2 per share -- for fundamental reasons that I've written about for a long time. I'm not a believer in Osiris' stem-cell therapy Prochymal because the clinical data are entirely unconvincing.