This blows Rexahn's claims of positive Archexin results out of the water. The 9.1-month median survival isn't real. Don't believe the data for a second.
@SCarolinaguy asks, "Of all the drugs approved or going through approval this year, which single one do you think will bring the most benefit to a patient?"
That's a really interesting question and one I don't think about often because I'm so focused on the investing, stock price, revenue potential, etc. side of things. It's also a difficult question to answer because benefit can be so subjective. Any drug that helps a patient is the most beneficial to them.
My choice for the most beneficial drug approved this year is Kalydeco, the cystic fibrosis drug developed by
(VRTX - Get Report)
. Kalydeco represents groundbreaking science that tackles the root cause of cystic fibrosis for the first time instead of just ameliorating the disease's symptoms. FDA approved Kalydeco in January.
I asked the Twitterverse to weigh in on their selection. Some people voted for eteplirsen, the Duchenne muscular dystrophy drug from
. A good choice but perhaps a bit premature since eteplirsen isn't approved yet and no one is really sure whether the data will allow Sarepta to file for early approval later this year.
Other nominees included Menhibrix, a meningococcal disease vaccine from
; Vascepa, the lipid-lowering prescription fish-oil pill from
; and naturally (although undeservingly) the obesity pills Belviq and Qsymia from
(ARNA - Get Report)
The question does allow for drugs are not yet approved buy may be before year's end. In this category, the blood-thinner Eliquis from
deserves consideration, says one Twitter follower. "Not as dramatic a benefit as Kalydeco but affects many more patients. Warfarin is a b--ch," he says.
Am I missing a truly beneficial new drug approved this year? Let me know.
--Written by Adam Feuerstein in Boston.
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